Current Stem Cell Benefits in Humans

Diseases Treatable With Adult Bone Marrow Stem Cells, Blood Stem Cells
or Umbilical Cord Blood Stem Cells Transplant

Sources include: www.bonemarrow.org; www.viacord.com;
www.cryo-cell.com

Diseases Treatable In Humans With Embryonic Stem Cells: NONE

 

Diseases Treatable with Adult Stem Cells:

Over 100 Acute Leukemias

• Acute Lymphoblastic Leukemia (ALL)
• Acute Myelogenous Leukemia (AML)
• Acute Biphenotypic Leukemia
• Acute Undifferentiated Leukemia
• Lymphomatoid granulomatosis
• Juvenile myelomonocytic Leukemia (JMML)

Chronic Leukemias

• Chronic Myelogenous Leukemia (CML)
• Chronic Lymphocytic Leukemia (CLL)
• Juvenile Chronic Myelogenous Leukemia (JCML) Myelodysplastic Syndromes
• Myelodysplastic Syndrome
• Refractory Anemia (RA)
• Refractory Anemia with Ringed Sideroblasts (RARS)
• Refractory Anemia with Excess Blasts (RAEB)
• Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
• Chronic Myelomonocytic Leukemia (CMML) Hematopoetic Cell Disorders
• Aplastic Anemia (Severe)
• Fanconi Anemia
• Paroxysmal Nocturnal Hemoglobinuria (PNH)
• Pure Red Cell Aplasia

Myeloproliferative Disorders

• Acute Myelofibrosis
• Agnogenic Myeloid Metaplasia (myelofibrosis)
• Polycythemia Vera
• Essential Thrombocythemia Lymphoproliferative Disorders
• Non-Hodgkin’s Lymphoma
• Hodgkin’s Disease Phagocyte Disorders
• Chediak-Higashi Syndrome
• Chronic Granulomatous Disease
• Neutrophil Actin Deficiency
• Reticular Dysgenesis

Inherited Metabolic Disorders

• Mucopolysaccharidoses (MPS)
• Hurler’s Syndrome (MPS-IH)
• Scheie Syndrome (MPS-IS)
• Hunter’s Syndrome (MPS-II)
• Sanfilippo Syndrome (MPS-III)
• Morquio Syndrome (MPS-IV)
• Maroteaux-Lamy Syndrome (MPS-VI)
• Sly Syndrome, Beta-Glucuronidase Deficiency (MPS-VII)
• Adrenoleukodystrophy
• Mucolipidosis II (I-cell Disease)
• Krabbe Disease
• Gaucher’s Disease
• Niemann-Pick Disease
• Wolman Disease
• Metachromatic Leukodystrophy Histiocytic Disorders
• Familial Erythrophagocytic Lymphohistiocytosis
• Histiocytosis-X
• Hemophagocytosis Inherited Erythrocyte Abnormalities
• Beta Thalassemia Major
• Sickle Cell Disease Inherited Immune System Disorders
• Ataxia-Telangiectasia
• Kostmann Syndrome
• Leukocyte Adhesion Deficiency
• DiGeorge Syndrome
• Bare Lymphocyte Syndrome
• Omenn’s Syndrome
• Severe Combined Immunodeficiency (SCID)
• SCID with Adenosine Deaminase Deficiency
• Absence of T & B Cells SCID
• Absence of T Cells, Normal B Cell SCID
• Common Variable Immunodeficiency
• Wiskott-Aldrich Syndrome
• X-Linked Lymphoproliferative Disorder

Anemias

• Congenital dyserythropoietic anemia
• Congenital sideroblastic anemia Additional Diseases
• Cyclic neutropenia
• Juvenile dermatomyositis
• Shwachman syndrome
• Thrombocytopenia with absent radius
• Autoimmune neutropenia (severe)
• HbSC disease
• Alpha mannosidosis
• Hermansky-Pudlak syndrome
Other Inherited Disorders
• Lesch-Nyhan Syndrome
• Cartilage-Hair Hypoplasia
• Glanzmann Thrombasthenia
• Osteopetrosis Inherited Platelet Abnormalities
• Amegakaryocytosis / Congenital Thrombocytopenia Plasma Cell Disorders
• Multiple Myeloma
• Plasma Cell Leukemia
• Waldenstrom’s Macroglobulinemia

Other Malignancies

• Breast Cancer
• Ewing Sarcoma
• Neuroblastoma
• Renal Cell Carcinoma
• Langerhan’s Cell Histiocytosis
• Severe Aplastic Anemia
• Diamond-Blackfan Anemia
• Dyskersis Congenita
• Amegakaryocytic Thrombocytopenia
• B- Thalassemia (Cooley’s Anemia)
• Liposarcoma
• Burkitt’s Lymphoma
• Batten disease (inherited neuronal ceroid lipofuscinosis)
• Gunther Disease
• Maroteaux-Lamy Syndrome
• Reticular Dysplasia
• Thymic Dysplasia
• Evans Syndrome
• E-Beta thalassemia
• E-Bo thalassemia
• Sickle Bo thalassemia
• Alpha thalassemia major (hydrops fetalis)
• Beta thalassemia intermedia
• Sandhoff syndrome
• Tay-Sachs Disease
• Adenosine deaminase deficiency
• IKK gamma deficiency
• X-linked agammaglobulinemia
• Immune dysregulation polyendocrineopathy